Tag: cmc

Ultragenyx Receives Complete Response Letter from FDA for UX111 AAV Gene Therapy to Treat Sanfilippo Syndrome Type A (MPS IIIA)

July 11, 2025 16:30 ET  | Source: Ultragenyx Pharmaceutical Inc. Complete Response…

GlobeNews Wire

RAEOA and CMC Ignite a New Chapter: Oecusse to Lead Timor-Lestes Modernization

OECUSSE, Timor-Leste--(BUSINESS WIRE)--  In a landmark display of visionary public-private collaboration, the…

Business Wire